Research Summaries December 2025
ALEX TLC (Alex, The Leukodystrophy Charity) produces monthly research summaries highlighting recent leukodystrophy research and…
ULF Awards $33,000 Research Grant to Advance Gene Therapy for H-ABC
The United Leukodystrophy Foundation (ULF) is proud to announce the award of a $33,000 research…
Research Summaries October 2025
ALEX TLC (Alex, The Leukodystrophy Charity) produces monthly research summaries highlighting recent leukodystrophy research and…
New Research: Endogenous Repair in Vanishing White Matter
A newly published article, “Endogenous Repair in Vanishing White Matter” explores how the brain may…
Research Summaries December 2025
ALEX TLC (Alex, The Leukodystrophy Charity) produces monthly research summaries highlighting recent leukodystrophy research and…
Positive Results Announced for Alexander Disease Clinical Trial
Ionis anounces positive topline results from pivotal study of zilganersen in Alexander disease The Ionis…
Minoxry Therapeutics: Leriglitazone has met the primary endpoint in NEXUS, the pivotal trial for pediatric patients with cALD
Press Release Summary (December 11, 2024): Minoryx Therapeutics, a late-stage biotech company, and Neuraxpharm Group,…
Viking Therapeutics Announces Results from Phase 1b Clinical Trial of VK0214 in Patients with X-ALD
Finding Answers, Finding Community: Tilyn’s Journey with TUBB4A Leukodystrophy
Finding Answers, Finding Community: Tilyn’s Journey with TUBB4A Leukodystrophy My name is Miesha Thomas, and…
Finding Our Village: Our Journey with Alexander Disease
Finding Our Village: Our Journey with Alexander Disease My name is Deb, and together with…
ULF Awards $33,000 Research Grant to Advance Gene Therapy for H-ABC
The United Leukodystrophy Foundation (ULF) is proud to announce the award of a $33,000 research…
Historic Expansion of Newborn Screening Includes MLD
Historic Expansion of Newborn Screening Includes Metachromatic Leukodystrophy (MLD) We are encouraged to share that…