Please note that events are listed for Central Time Zone (Chicago). Upcoming Events Oct 27 Featured Featured 12:00 pm - 1:00 pm Caregivers Support Group Nov 24 Featured Featured 1:00 pm - 2:00 pm Caregivers Support Group Dec 8 Featured Featured 12:00 pm - 1:00 pm Caregivers Support Group View Calendar Recent Posts PMD Clinical Study Aspa Therapeutics: A Study of AAV9 Gene Therapy in Children With Canavan Disease Aspa Therapeutics: A Natural History Study of Patients With Canavan Disease BridgeBio press release about the RMAT designation for the Aspa clinical trial in Canavan Disease CTX Patient Assistance Program is open and accepting assistance applications In Memorial and Honor: May – July 2024 An Update from Passage Bio on Out-Licensing of Pediatric Programs to GEMMA Biotherapeutics In Memorial and Honor – April 2024 Calyx: New Clinical Trial in cALD PMD Interview Study Opportunity Recruiting Now Read More News Share your story Read Stories
