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Poxel Announces New Strategic Direction with Increasing Focus on Rare Metabolic Diseases Following Recent Achievements

Download as PDF July 12, 2021 Following the recent approval of TWYMEEG® (Imeglimin) in Japan and associated potential future revenues, Poxel to accelerate and expand rare metabolic disease programs leveraging existing platforms and proven capabilities Poxel to advance its deuterated thiazolidinediones (dTZD) and direct adenosine monophosphate-activated protein kinase (AMPK) activator platforms in rare metabolic diseases …

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FDA Clearance of Investigational New Drug for Patients with Krabbe Disease

January 4, 2021 by Dan Salvo Forge Biologics has received IND, IBC, and IRB clearance for FBX-101, a gene therapy for patients with Krabbe disease, a rare and fatal genetic disorder FBX-101 is a first-in-human potential treatment utilizing an adeno-associated virus (AAV) to deliver a functioning copy of the GALC gene to cells in the CNS and …

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In Memorial or Honorarium – August 2020

The ULF received donations in memorial or honorarium for the following during the month of August 2020. We apologize for any inadvertent omittance or misspellings. Please notify us if we have made a mistake at office@ulf.org or by calling 815.748.3211. IN HONOR OF Amie Matlon: Marianne Matlon  Aveline Brendel: Pauline Naudin, William Brendel, Amy McKenzie, Ryan McKenzie, …

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In Memorial or Honorarium – July 2020

The ULF received donations in memorial or honorarium for the following during the month of July 2020. We apologize for any inadvertent omittance or misspellings. Please notify us if we have made a mistake at office@ulf.org or by calling 815.748.3211. IN HONOR OF David Stocki: Melissa Scier – For my son who has Alexander Disease Leukodystrophy  Dax …

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