Please note that events are listed for Central Time Zone (Chicago). Upcoming Events Nov 24 Featured Featured 1:00 pm - 2:00 pm Caregivers Support Group Dec 1 Featured Featured 1:00 pm - 2:00 pm Mental Health Over the Holidays – WEBINAR Dec 8 Featured Featured 12:00 pm - 1:00 pm Caregivers Support Group View Calendar Recent Posts Experiences of mothers of long-term surviving patients with cerebral adrenoleukodystrophy: a qualitative study Gene therapy shows long-term benefit for patients with Cerebral adrenoleukodystrophy (CALD) Viking Therapeutics Announces Results from Phase 1b Clinical Trial of VK0214 in Patients with X-ALD BridgeBio Shares Positive Data from Canavan Disease Study In Memorial and Honor: August – September 2024 PMD Clinical Study Aspa Therapeutics: A Study of AAV9 Gene Therapy in Children With Canavan Disease Aspa Therapeutics: A Natural History Study of Patients With Canavan Disease BridgeBio press release about the RMAT designation for the Aspa clinical trial in Canavan Disease CTX Patient Assistance Program is open and accepting assistance applications Read More News Share your story Read Stories
