Please note that events are listed for Central Time Zone (Chicago). Upcoming Events Mar 24 12:30 pm - 1:30 pm Caregivers Support Group Apr 21 12:00 pm - 1:00 pm Caregivers Support Group May 26 1:00 pm - 2:00 pm Caregivers Support Group Jun 16 12:00 pm - 1:00 pm Caregivers Support Group: Father’s Day Group Jul 28 1:00 pm - 2:00 pm Caregivers Support Group View Calendar Recent Posts FDA Approves First Gene Therapy for Children with Metachromatic Leukodystrophy In Memorial and Honor – February 2024 Two ALSP Studies Now Recruiting In Memorial and Honor – January 2024 Forge Biologics Announces Positive FBX-101 Clinical Trial Update in Patients with Krabbe Disease Identified by Newborn Screening Ahead of RUSP Vote In Memorial and Honor – December 2023 Daniil’s Story In Memorial and Honor – November 2023 In Memorial and Honor – October 2023 Minoryx Announces Patient Enrollment of their CALYX Trial Read More News Share your story Read Stories