upcoming events

Event Information:

  • Wed

    Gene Therapy Webinar

    12:00 pmwebinar

    Metabol!c Support UK

    Learn about the new gene therapy currently being developed for NKH and ASA, and future developments may also be suitable for those living with other conditions including MSUD, PFIC2, MMA, PA and OTC.


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Sam Buck, VWM

“Until February 2013, our 2-year-old son Sam was completely normal child, no problems with his pregnancy or birth, he met every milestone, and overall was…
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