Conference

Each year, the NORD Summit, one of the largest multi-stakeholder events in rare disease, brings together participants spanning the rare community, including rare disease experts and leaders from patient advocacy groups, government, industry, and academia to discuss the most current and critical topics related to rare diseases and orphan products. https://nordsummit.org/

The EPNS Congress provides an opportunity to learn about the latest developments in the rapidly evolving field of child neurology, including basic science, diagnostic methods, and novel treatments. You can network with colleagues and industry partners all focused on delivering the best possible care for children with neurological disorders.https://epns-congress.com/

The Rare Drug Development Symposium, in partnership with the Orphan Disease Center of the University of Pennsylvania, brings together rare disease advocacy leaders and researchers to identify barriers to research, envision solutions, and accelerate progress for our communities. This two-day, in-person-only summit offers a unique opportunity to engage in interactive small-group workshops with experts and …

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The European Conference on Rare Diseases and Orphan Products is recognised globally as the largest, patient-led rare disease event in which collaborative dialogue, learning and conversation takes place, forming the groundwork to shape future rare disease policies. Please contact martina.bergna@eurordis.org for more information.

The Hunter’s Hope Medical and Family Symposium is a time for Leukodystrophy families, medical providers, newborn screening lab personnel, industry partners, and researchers from around the world to gather for learning, sharing, and Hope.